Combined neoadjuvant and adjuvant therapy versus adjuvant therapy in high-risk upper tract Urothelial carcinoma: a propensity matched multicenter analysis of robust 2.0 international collaborative group

Document Type

Conference Proceeding

Publication Date

3-1-2025

Publication Title

Eur Urol

Abstract

Introduction & Objectives: Combined neoadjuvant and adjuvant therapy (CNAAT) has shown potential survival benefits in urothelial carcinoma (UC) of the bladder, but its efficacy in upper tract UC (UTUC) is unclear. High-risk features—clinical stage 2 T3, node-positive disease, multifocality, high-grade pathology, hydronephrosis, and large tumor size— are associated with poor prognosis in UTUC. We investigated the oncological outcomes of CNAAT versus adjuvant therapy (AT) alone in high-risk UTUC patients who underwent nephroureterectomy (NU). Materials & Methods: We conducted a retrospective analysis of 1,718 patients who underwent NU for UTUC between 2015 and 2023 at 17 centers across the United States, Europe, and Asia. High-risk patients were identified based on the above criteria. Propensity score matching based on pathological T/N stages, resulting in 90 matched patients: 45 receiving CNAAT and 45 receiving AT. Kaplan-Meier survival curves and Cox proportional hazards models were employed to assess overall survival (OS), cancer-specific survival (CSS), metastasis-free survival (MFS), and recurrence-free survival (RFS). Results: The matched cohort had advanced pathological stages, with 69% having pathological T3/T4 tumors and 18% nodal involvement, with a median follow-up of 18 months. After adjusting for variables, CNAAT and AT groups had comparable oncological outcomes: 2-year OS (72% vs. 74%; p = 0.85), CSS (76% vs. 85%; p = 0.43), RFS (43% vs. 40%; p = 0.84), or MFS (44% vs. 48%; p = 0.89). Cox regression indicated that CNAAT did not confer a significant survival advantage over AT after adjusting for clinical and pathological factors (HR for OS: 1.15; p = 0.72). Conclusions: In this large multicenter international cohort, CNAAT did not show a significant advantage over AT alone in patients with high-risk UTUC. Larger prospective studies with longer follow-up are needed to clarify the role of multimodal therapy in UTUC management.[Figure presented].

Volume

87

Issue

S1

First Page

866

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